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adolescent
article
clinical article
female
human
40
adult
38
Adolescent
32
Female
32
male
32
controlled study
28
Adult
26
Male
24
Humans
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priority journal
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aged
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Argentina
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child
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Aged
10
Child
10
Human
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Middle Aged
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Child, Preschool
6
Genotype
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Infant
6
Middle Age
6
Mutation
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Support, Non-U.S. Gov't
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Young Adult
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disease severity
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drug efficacy
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